Table 1:

Cohort demographics

Discovery Cohort Stanford (n = 47) (%)Validation Cohort Toronto (n = 52) (%)
Sex
    Male33 (70)28 (54)
    Female14 (30)24 (46)
Age (yr)
    Median (range)8.2 (0.9–33.9)7.9 (1–1–15.2)
    0–35 (11)5 (10)
    >3–1637 (78)46 (88)
    >165 (11)1 (2)
Histology
    LCA10 (21)4 (8)
    Classic31 (66)37 (71)
    Desmoplastic4 (9)11 (21)
    Other2 (4)0
Subgroup
    WNT4 (8)10 (19)
    SHH13 (28)11 (21)
    Group 313 (28)12 (23)
    Group 417 (36)19 (37)
  • Note:—LCA indicates large-cell anaplastic.