User profiles for V. Dangouloff

Volodia Dangouloff-Ros

Pediatric Radiology, Hôpital Necker Enfants Malades, Paris, France
Verified email at aphp.fr
Cited by 1119

Clinical evidence supporting early treatment of patients with spinal muscular atrophy: current perspectives

T Dangouloff, L Servais - Therapeutics and clinical risk …, 2019 - Taylor & Francis
Recent advances in the treatment of spinal muscular atrophy (SMA) have dramatically altered
prognosis. Rather than a rapidly lethal disease, SMA type 1, the most severe form with the …

[HTML][HTML] Systematic literature review of the economic burden of spinal muscular atrophy and economic evaluations of treatments

T Dangouloff, C Botty, C Beaudart, L Servais… - Orphanet Journal of …, 2021 - Springer
Background Spinal muscular atrophy (SMA) is a rare and devastating condition for which
new disease-modifying treatments have recently been approved. Given the increasing …

EANO–EURACAN clinical practice guideline for diagnosis, treatment, and follow-up of post-pubertal and adult patients with medulloblastoma

…, RD Kortmann, J Bromberg, V Dangouloff-Ros… - The Lancet …, 2019 - thelancet.com
The European Association of Neuro-Oncology (EANO) and EUropean RAre CANcer (EURACAN)
guideline provides recommendations for the diagnosis, treatment, and follow-up of post…

Neuroimaging manifestations in children with SARS-CoV-2 infection: a multinational, multicentre collaborative study

…, PPDA Coimbra, V Dangouloff-Ros… - The Lancet Child & …, 2021 - thelancet.com
Background The CNS manifestations of COVID-19 in children have primarily been described
in case reports, which limit the ability to appreciate the full spectrum of the disease in …

Newborn screening programs for spinal muscular atrophy worldwide: Where we stand and where to go

T Dangouloff, E Vrščaj, L Servais, D Osredkar… - Neuromuscular …, 2021 - Elsevier
Spinal muscular atrophy (SMA) is a rare and devastating disease. New disease-modifying
treatments have recently been approved and early treatment has been related to a better …

Arterial spin labeling to predict brain tumor grading in children: correlations between histopathologic vascular density and perfusion MR imaging

V Dangouloff-Ros, C Deroulers, F Foissac, M Badoual… - Radiology, 2016 - pubs.rsna.org
Purpose To compare arterial spin labeling (ASL) data between low- and high-grade brain
tumors in children to establish a cutoff to distinguish low- from high-grade neoplasms and to …

[HTML][HTML] Three years pilot of spinal muscular atrophy newborn screening turned into official program in Southern Belgium

…, S Huybrechts, B Mast, R van Olden, T Dangouloff… - Scientific reports, 2021 - nature.com
Three new therapies for spinal muscular atrophy (SMA) have been approved by the United
States Food and Drug Administration and the European Medicines Agency since 2016. …

Newborn screening for SMA in Southern Belgium

…, V Bours, M Hiligsmann, T Dangouloff… - Neuromuscular …, 2019 - Elsevier
Approval was recently granted for a new treatment for spinal muscular atrophy (SMA). Given
that the treatment is effective when administered early and the societal burden of SMA-…

244th ENMC international workshop: newborn screening in spinal muscular atrophy May 10–12, 2019, Hoofdorp, The Netherlands

T Dangouloff, A Burghes, EF Tizzano, L Servais… - Neuromuscular …, 2020 - Elsevier
A total of 19 participants including clinicians, newborn screening specialists, economists,
geneticists, patients and patient advocates, and industry representatives from 12 countries …

Financial cost and quality of life of patients with spinal muscular atrophy identified by symptoms or newborn screening

T Dangouloff, M Hiligsmann… - … Medicine & Child …, 2023 - Wiley Online Library
Aim To compare the societal financial costs and quality of life (QoL) of untreated patients
with spinal muscular atrophy (SMA) and treated patients identified because they presented …